Human Gene Therapy

Volume 32, Issue 7/8 / April 2021 

Latest Impact Factors: 4.510

In this issue of Human Gene Therapy on the occasion of the 2021 American Society for Gene Therapy Annual Meeting, we chose to highlight a few of the other outstanding scientist in our field whose articles are published here. See featured articles below, and access the full issue here!

Read and share articles from this special issue:

Women Lead Gene Therapy Science in 2021

Jennifer E. Adair, Karla Shepard Rubinger, and Terence R. Flotte  Read Now

Mavis Agbandje-McKenna's Lifelong Commitment to Teaching and Research
Barry J. Byrne, Angela L. McCall, Beverly L. Davidson, and R. Jude Samulski  Read Now

A Beautiful Mind and the Heart of an Explorer
Read Now

Keys to Delivery: An Interview with Hildegard Büning
Kevin Davies  Read Now

Linking the Expression of Therapeutic Genes to Unfolded Protein Response: A New Option for Anti-Hepatitis B Virus Gene Therapy
Estanislao Nistal-Villán, Josepmaria Argemi, Anchel de Jaime-Soguero, Roberto Ferrero, Marianna di Scala, Estefania Rodriguez-Garcia, Aniol Coll, Sergio Rius-Rocabert, Jesús Prieto, Gloria González-Aseguinolaza, and Tomás Aragón  Read Now

The Challenge of Gene Therapy for Neurological Diseases: Strategies and Tools to Achieve Efficient Delivery to the Central Nervous System
Françoise Piguet, Timothée de Saint Denis, Emilie Audouard, Kevin Beccaria, Arthur André, Guillaume Wurtz, Raphael Schatz, Sandro Alves, Caroline Sevin, Michel Zerah, and Nathalie Cartier  Read Now

[ Open Access ]
Dose-Escalation Study of Systemically Delivered rAAVrh74.MHCK7.micro-dystrophin in the mdx Mouse Model of Duchenne Muscular Dystrophy
Rachael A. Potter, Danielle A. Griffin, Kristin N. Heller, Ellyn L. Peterson, Emma K. Clark, Jerry R. Mendell, and Louise R. Rodino-Klapac  Read Now


The Rosalind Franklin Society recognizes and celebrates the contributions of outstanding women in the life sciences and affiliated disciplines, promotes broadened opportunities for women in the sciences, and through its many activities motivates new generations of women to this calling.  The Society honors the achievements of Rosalind Franklin (1920-1958), a British x-ray crystallographer whose extraordinary work, though largely overlooked and under-appreciated at the time, was crucial to the discovery of DNA’s structure by James Watson and Francis Crick.  The powerful symbolism of her remarkable story drives the Society’s agenda.

The Rosalind Franklin Society is a tax-exempt 501(c)(3).